Speakers

Carlos Almeciga, BPharm, PhD
Colombia
Pontificia Universidad Javeriana

Michael Beck, MD
Germany
Children’s Hospital at University of Mainz

Brian Bigger, PhD
United Kingdom
The University of Manchester

Melissa Bilodeau
Canada
MPS IVA Patient

Stephanie Bozarth, MSW
United States
Chairman, Board of Directors, National MPS Society

Barbara Burton, MD
United States
Ann & Robert H. Lurie Children’s Hospital of Chicago

Lorne Clarke, MD
Canada
British Columbia Children’s Hospital

Olivier Danos, PhD
United States
CSO, REGENXBIO

Beverly Davidson, PhD
United States
Children’s Hospital of Philadelphia

Camila de Britto Para de Aragao
Canada
McGill University CHU Sainte-Justine Research Center

Patricia Dickson, MD
United States
Harbor- UCLA Medical Center
Los Angeles Biomedical Research Institute

Deborah Eastwood, MB, ChB, FRCS
United Kingdom

Martin Egeland, PhD
United States
LA Biomed

Julie Eisengart, PhD, LP
United States
University of Minnesota

Richard Gallo, MD, PhD
United States
University of California, San Diego

Michael H. Gelb, PhD
United States
University of Washington

Robert Giugliani, MD, PhD
Brazil
UFRGS and HCPA, Porto Alegre

Philip Gordts, PhD
United States
University of California, San Diego

Steven Gray, PhD
United States
University of TX Southwestern Medical Center

Paul Harmatz, MD
United States
Children’s Hospital of Oakland

Kim Hemsley, PhD
Australia
Childhood Dementia Research Group, HCN, SAHMRI

Stacy Hewson, MS, MSc, CCGC, CGC
Canada
The Hospital for Sick Children, Toronto

Melissa Hogan
United States
President, Project Alive

Rebecca Holley
United Kingdom
University of Manchester

Dafne Horovitz
Brazil
Instituto Fernandes Figueira / Fiocruz

Simon Jones, MD
United Kingdom
Saint Mary’s Hospital, Central Manchester University Hospitals NHS Foundation Trust

Emil Kakkis, MD, PhD
United States
President/CEO, Ultragenyx
EveryLife Foundation

Shih-Hsin Kan, PhD
United States
LA BioMedical Research Institute at Harbor-UCLA

Terri Klein,
NPGC
United States
President/CEO, National MPS Society

Heather Lau
United States
New York University Langone Medical Center

Sara Marco Costa, PhD
Spain
CBATEG, Universitat Autònoma de Barcelona, Department of Biochemistry and Molecular Biology

Tim Miller, PhD
United States
CEO, Abeona Therapeutics

Enrico Moro, PhD
Italy
University of Padova

Nicole Muschol, PhD
Germany
University Medical Center Hamburg-Eppendorf

Joseph Muenzer, MD, PhD
United States
The University of North Carolina at Chapel Hill

Jama Nateqi, PhD
Austria
Symptoma GmbH

Igor Nestrasil, MD, PhD
United States
University of Minnesota

Stephanie Nijmeijer, MD
Netherlands
University of Padova

Torayuki Okuyama, MD, PhD
Japan
National Center for Child Health and Development

Paul Orchard, MD
United States
University of Minnesota

Xuefang Pan, PhD
Canada
Division of Medical Genetics, Sainte-Justine University Hospital Research Center, University of Montreal

Helen Parker
United Kingdom
University of Manchester

Frances Platt, PhD, FMedSci
United Kingdom
University of Oxford

Anya Prince, MPP, JD
United States
University of Iowa Law

Mathias Schmidt, PhD
United States
CEO, ArmaGen, Inc.

Elsa Shapiro, PhD, ABPP
United States
University of Minnesota

Larry Sherman, PhD
United States
Oregon National Primate Research Center
Oregon Health and Science University

Calogera Simonaro, PhD

United States
Icahn School of Medicine at Mount Sinai

Raj Singh, PhD
United States
Baebies, Inc.

Bob Stevens
United Kingdom
Group Chief Executive, MPS Society UK

Adrian Thrasher, PhD MB BS FSB FMedSci FRCP FRCPath FRCPCH
United Kingdom
UCL Great Ormond Street Institute of Child Health in Paediatric Immunology

Shunji Tomatsu, MD, PhD
United States
Nemours /Alfred I. duPont Hospital for Children

Kevin Walker, MD
United States
Gillette Children’s Specialty Healthcare

Raymond Wang, MD
United States
Children’s Hospital of Orange County

Jacob Wesley, Pharm. D
United States
Regenxbio

Klane White, MD, MS
United States
Seattle Children’s Hospital

Chester Whitley, MD, PhD
United States
University of Minnesota